QR Code (код быстрого отклика)

Burosumab in infants with X-linked hypophosphatemic rickets: a case series

Abstract Background X-linked hypophosphatemic rickets (XLH) is a rare inherited metabolic bone disorder caused by excess fibroblast growth factor 23 (FGF23), leading to hypophosphatemia and rickets. Burosumab, a human monoclonal antibody targeting FGF23, was approved for the treatment of XLH in Apri...

Полное описание

Сохранить в:
Библиографические подробности
Главные авторы: Ravit Regev, Avivit Brener, Nitzan Dror, Raphael Krespi, Rebeca Rapalino, Efrat Chorna, Ophir Borger, Adar Lopez, Yael Lebenthal, Leonid Zeitlin
Формат: Artigo
Язык:Inglês
Опубликовано: BMC 2026-01-01
Серии:Orphanet Journal of Rare Diseases
Предметы:
Online-ссылка:https://doi.org/10.1186/s13023-025-04177-2
Метки: Добавить метку
Нет меток, Требуется 1-ая метка записи!