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Real-world evidence study finds no new-onset diabetes or drug-related hyperglycemia in Pompe disease patients treated with avalglucosidase alfa

Avalglucosidase alfa therapy for Pompe disease is diluted in dextrose 5% solution in water (D5W) for infusion, which raises questions about the potential for hyperglycemia or worsening diabetes. Using United States insurance claims data, we assessed the impact of biweekly infusions on hyperglycemia,...

Täydet tiedot

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Bibliografiset tiedot
Päätekijät: Alexandra Dumitriu, Ann Lucas, Raffaella Colzani
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: Elsevier 2024-03-01
Sarja:Molecular Genetics and Metabolism Reports
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Linkit:http://www.sciencedirect.com/science/article/pii/S221442692400017X
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