Restoration of brain dystrophin using tricyclo-DNA ASOs restores neurobehavioral deficits in DMD mice

Lignende værker

• Networking to Optimize <i>Dmd</i> exon 53 Skipping in the Brain of <i>mdx52</i> Mouse Model
  af: Mathilde Doisy, et al.
  Udgivet: (2023-12-01)
• Oligonucleotide Enhancing Compound Increases Tricyclo-DNA Mediated Exon-Skipping Efficacy in the Mdx Mouse Model
  af: Flavien Bizot, et al.
  Udgivet: (2023-02-01)
• Rational Design of Chimeric Antisense Oligonucleotides on a Mixed PO–PS Backbone for Splice-Switching Applications
  af: Bao T. Le, et al.
  Udgivet: (2024-07-01)
• In Vitro Studies to Evaluate the Intestinal Permeation of an Ursodeoxycholic Acid-Conjugated Oligonucleotide for Duchenne Muscular Dystrophy Treatment
  af: Marika Faiella, et al.
  Udgivet: (2024-08-01)
• Intramuscular Evaluation of Chimeric Locked Nucleic Acid/2′<i>O</i>Methyl-Modified Antisense Oligonucleotides for Targeted Exon 23 Skipping in Mdx Mice
  af: Michaella Georgiadou, et al.
  Udgivet: (2021-10-01)