Knock-out of specific DMD gene isoforms in the parental hESC line SA001 using CRISPR/Cas9

The DMD gene, which encodes the protein dystrophin, is involved in a group of diseases known as dystrophinopathies, which includes Duchenne Muscular Dystrophy (DMD). DMD is a progressive and lethal muscular disorder mainly affecting boys that results from the loss of function of the longer dystrophi...

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Prif Awduron:	Laure Chatrousse, Thifaine Poullion, Hamel Mahiou, Lina El-Kassar, Karine Giraud-Triboult, Claire Boissart, Alexandra Benchoua
Fformat:	Artigo
Iaith:	Inglês
Cyhoeddwyd:	Elsevier 2026-02-01
Cyfres:	Stem Cell Research
Mynediad Ar-lein:	http://www.sciencedirect.com/science/article/pii/S1873506125002491
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