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Concizumab prophylaxis in a 2-year-old patient with severe hemophilia B and inhibitor: a case report

Hemophilia B is a rare X-linked congenital bleeding disorder characterized by a deficiency in coagulation factor IX (FIX). Standard management relies on exogenous factor replacement; however, the development of neutralizing alloantibodies (inhibitors) against infused clotting factor can significantl...

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Autori principali: Mandy Yuan, Sanober Nusrat, Osman Khan
Natura: Artigo
Lingua:Inglês
Pubblicazione: Frontiers Media S.A. 2026-07-01
Serie:Frontiers in Pharmacology
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Accesso online:https://www.frontiersin.org/articles/10.3389/fphar.2026.1876168/full
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