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Clinical Outcomes and Disease Management for Patients with Paroxysmal Nocturnal Haemoglobinuria in China: Results from a Real-World Study

Abstract Background Paroxysmal nocturnal haemoglobinuria (PNH) is a chronic haematological disorder caused by uncontrolled complement activation, leading to intravascular haemolysis, indicated by increased lactate dehydrogenase levels (LDH). Standard-of-care complement factor 5 inhibitors have only...

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Principais autores: Rong Fu, Hui Liu, Pin-Tzu Su, Xuefei Liu, Karl-Johan Myrén, Francesca Gatta, Lucy Earl, Yasmin Taylor, Alice Simons, Elmira Lechat
Format: Artigo
Sprog:Inglês
Udgivet: Adis, Springer Healthcare 2025-08-01
Serier:Drugs - Real World Outcomes
Online adgang:https://doi.org/10.1007/s40801-025-00512-y
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