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The role of transferrin receptors in crossing the blood-brain barrier in the treatment of mucopolysaccharidosis

Background. Currently, in Russia, intravenous enzyme replacement therapy is used for the treatment of mucopolysaccharidosis type II. In recent months, enzyme replacement therapy administered via the cerebral ventricles (intracerebroventricular administration) has become available. The main drawback...

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Principais autores: Larisa I. Minaycheva, Gulnara N. Seitova, Ekaterina A. Shatokhina
格式: Artigo
語言:Russo
出版: Open Systems Publication 2026-04-01
叢編:Лечащий Врач
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在線閱讀:https://journal.lvrach.ru/jour/article/view/1592
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