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Evolution of Clinical Trial Design in ADPKD

Autosomal Dominant Polycystic Kidney Disease (ADPKD) is characterized by continuous growth in the size and number of kidney cysts during decades of relatively preserved renal function. Because of this slow progression, traditional clinical trial design, focused on kidney functional outcomes such as...

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Autors principals: John R. Roth, Neera K. Dahl, Pranav S. Garimella
Format: Artigo
Idioma:Inglês
Publicat: Elsevier 2026-04-01
Col·lecció:Kidney International Reports
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Accés en línia:http://www.sciencedirect.com/science/article/pii/S2468024926000173
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