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Derivation of iPSC line (RCMGi002-A) from dermal fibroblasts of a cystic fibrosis female patient with homozygous F508del mutation

Cystic fibrosis is one of the most common inherited diseases caused by mutations in CFTR gene, of which F508del is the most frequent. Currently, the possibility of cell therapy including genome editing is widely discussed. We generated induced pluripotent stem cells from fibroblasts obtained from a...

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Hlavní autoři: Ekaterina Kondrateva, Anna Demchenko, Yana Slesarenko, Matvey Yasinovsky, Elena Amelina, Viacheslav Tabakov, Ekaterina Voronina, Alexander Lavrov, Svetlana Smirnikhina
Médium: Artigo
Jazyk:Inglês
Vydáno: Elsevier 2021-05-01
Edice:Stem Cell Research
On-line přístup:http://www.sciencedirect.com/science/article/pii/S1873506121000970
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