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Nanotube-Assisted Motor Neuron and Neuromuscular Junction Stabilization in Spinal Muscular Atrophy: A Hypothesis for Adjunctive Therapy

Spinal muscular atrophy (SMA) therapies that restore SMN expression improve survival and motor function but often fail to fully stabilize distal motor units or sustain endurance. We propose a hypothesis-driven adjunctive approach, intended to complement SMN-restoring therapies, in which localized na...

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Autors principals: Almir Fajkić, Andrej Belančić, Kristina Pilipović, Valentino Rački, Silvestar Mežnarić, Tamara Janković, Elvira Meni Maria Gkrinia, Dinko Vitezić, Jasenka Mršić-Pelčić
Format: Artigo
Idioma:Inglês
Publicat: MDPI AG 2026-05-01
Col·lecció:Neurology International
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Accés en línia:https://www.mdpi.com/2035-8377/18/5/87
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