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GENETIC AND NON-GENETIC DETERMINANTS OF SUCCESSFUL IMMUNE TOLERANCE INDUCTION IN PEOPLE WITH SEVERE HEMOPHILIA A

Background: Eradicating inhibitors to restore the effectiveness of Factor VIII (FVIII) is a desirable treatment goal for People with Severe Hemophilia A (PwSHA) and inhibitors, as this enables treatment of bleeding episodes with FVIII concentrates. However, since Immune Tolerance Induction (ITI) is...

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Autores principales: I Oomen, RM Camelo, M Carcao, G Castaman, JCJ Eikenboom, K Fischer, WG Frank Leebeek, D Lillicrap, ME Mancuso, D Matino, DMN Di Minno, AB Mohseny, J Oldenburg, SM Rezende, GE Rivard, N Rydz, S Schols, Voorberg Jan, FMRA Callado, LEM Carvalho, VKB Franco, CS Lorenzato, K Fijnvandraat, S Gouw
Formato: Artigo
Lenguaje:Inglês
Publicado: Elsevier 2024-10-01
Colección:Hematology, Transfusion and Cell Therapy
Acceso en línea:http://www.sciencedirect.com/science/article/pii/S253113792401277X
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