Quality of life improvements following one year of setmelanotide in children and adult patients with Bardet–Biedl syndrome: phase 3 trial results

Abstract Background Bardet–Biedl syndrome is a rare genetic disease associated with hyperphagia and early-onset, severe obesity. There is limited evidence on how hyperphagia and obesity affect health-related quality of life in patients with Bardet–Biedl syndrome, and on how management of these sympt...

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Principais autores:	Elizabeth Forsythe, Robert M. Haws, Jesús Argente, Philip Beales, Gabriel Á. Martos-Moreno, Hélène Dollfus, Costel Chirila, Ari Gnanasakthy, Brieana C. Buckley, Usha G. Mallya, Karine Clément, Andrea M. Haqq
格式:	Artigo
语言:	Inglês
出版:	BMC 2023-01-01
丛编:	Orphanet Journal of Rare Diseases
主题:	BBS Genetic obesity IWQOL-Lite PedsQL Quality of life Setmelanotide
在线阅读:	https://doi.org/10.1186/s13023-022-02602-4
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