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Efficacy and safety of thalidomide in children with monogenic autoinflammatory diseases: a single-center, real-world-evidence study

Abstract Background Monogenic autoinflammatory diseases (AIDs) are rare inflammatory diseases caused by genetic variants. The pathogenesis is complex and treatment options are limited. This study aimed to describe the safety and efficacy of thalidomide in the treatment of monogenic AIDs. Methods Thi...

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Autori principali: Caihui Zhang, Zhongxun Yu, Sihao Gao, Mingsheng Ma, Lijuan Gou, Changyan Wang, Lin Wang, Ji Li, Linqing Zhong, Yu Zhou, Wei Wang, Hongmei Song
Natura: Artigo
Lingua:Inglês
Pubblicazione: BMC 2023-10-01
Serie:Pediatric Rheumatology Online Journal
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Accesso online:https://doi.org/10.1186/s12969-023-00881-0
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