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Zebrafish Models of Diamond-Blackfan Anemia: A Tool for Understanding the Disease Pathogenesis and Drug Discovery

Diamond-Blackfan anemia (DBA) is a rare bone marrow failure syndrome characterized by red blood cell aplasia. Currently, mutations in 19 ribosomal protein genes have been identified in patients. However, the pathogenic mechanism of DBA remains unknown. Recently, several DBA models were generated in...

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Autori principali: Tamayo Uechi, Naoya Kenmochi
Natura: Artigo
Lingua:Inglês
Pubblicazione: MDPI AG 2019-10-01
Serie:Pharmaceuticals
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Accesso online:https://www.mdpi.com/1424-8247/12/4/151
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