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Optimizing pediatric ITP therapy: a real-world study on plasma concentration-guided eltrombopag dosing

Abstract Eltrombopag (ELT) is a second-line therapy for pediatric immune thrombocytopenia (ITP), but inter-individual variability in metabolism leads to wide plasma concentration differences at the same dose, affecting efficacy and adverse drug reactions (ADRs). To validate the feasibility of indivi...

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Autors principals: Jia Li, Bo Liu, Nan Wang, Shuyue Dong, Jingyao Ma, Xiaoling Wang, Peng Guo, Runhui Wu, Xiaoling Cheng
Format: Artigo
Idioma:Inglês
Publicat: Springer 2026-03-01
Col·lecció:Annals of Hematology
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Accés en línia:https://doi.org/10.1007/s00277-026-06875-8
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