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Efficacy and safety of CFTR modulators in patients with interstitial lung disease caused by ABCA3 transporter deficiency

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Bibliografiske detaljer
Principais autores: Mathilde Le Brun, Nadia Nathan, Camille Louvrier, Marie Legendre, Severine Feuillet, Justine Frija-Masson, Mwetty Onanga, Lise Morer, Marie-Pierre Debray, Isabelle Fajac, Pierre-Régis Burgel, Sylvain Marchand-Adam, Bruno Crestani, Raphaël Borie
Format: Artigo
Sprog:Inglês
Udgivet: European Respiratory Society 2025-03-01
Serier:ERJ Open Research
Online adgang:http://openres.ersjournals.com/content/11/2/00701-2024.full
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