Expression and function of four AAV-based constructs for dystrophin restoration in the mdx mouse model of Duchenne muscular dystrophy

類似資料

• The X‐linked Becker muscular dystrophy (bmx) mouse models Becker muscular dystrophy via deletion of murine dystrophin exons 45–47
  著者:: Christopher R. Heier, 等
  出版事項: (2023-04-01)
• Systemic delivery of an AAV9 exon-skipping vector significantly improves or prevents features of Duchenne muscular dystrophy in the Dup2 mouse
  著者:: Nicolas Wein, 等
  出版事項: (2022-09-01)
• Molecular Characterization of Dystrophin Gene in Iraqi Patients with Muscular Dystrophy.
  著者:: Areen T. Ramadhan Al-Hadithi, 等
  出版事項: (2014-07-01)
• Casimersen (AMONDYS 45™): An Antisense Oligonucleotide for Duchenne Muscular Dystrophy
  著者:: Milyard Assefa, 等
  出版事項: (2024-04-01)
• The Multi-System Roles of Dp71 Dystrophin Isoforms in Duchenne Muscular Dystrophy
  著者:: Harry Wilton-Clark, 等
  出版事項: (2026-06-01)