Fibrodysplasia ossificans progressiva: from clinical complexity to therapeutic opportunity
Abstract Fibrodysplasia Ossificans Progressiva (FOP) is an ultra-rare and severely disabling genetic disorder affecting approximately one in two million individuals worldwide. It is characterised by progressive endochondral heterotopic ossification (HO), in which ectopic cartilage formation precedes...
Kaydedildi:
| Asıl Yazarlar: | , , , , , , |
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| Materyal Türü: | Artigo |
| Dil: | Inglês |
| Baskı/Yayın Bilgisi: |
Springer
2026-01-01
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| Seri Bilgileri: | Journal of Rare Diseases |
| Konular: | |
| Online Erişim: | https://doi.org/10.1007/s44162-025-00144-4 |
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