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Towards a sustainable rare disease and orphan drug ecosystem in Saudi Arabia: policy insights from a multi-stakeholder workshop

IntroductionRare diseases (RDs) present significant challenges worldwide, including Saudi Arabia (SA), where access to orphan drugs (ODs) is suboptimal. This study summarizes key insights from a multi-stakeholder workshop conducted in SA to explore and address challenges related to RD and OD accessi...

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Principais autores: Ghada Mohammed Abozaid, Hussain Abdulrahman Al-Omar, Abdulaziz Alrabiah, Asma AlMuaither, Amy Jayne McKnight
Formato: Artigo
Idioma:Inglês
Publicado: Frontiers Media S.A. 2025-05-01
Series:Frontiers in Pharmacology
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Acceso en liña:https://www.frontiersin.org/articles/10.3389/fphar.2025.1583477/full
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