Diving into progress: a review on current therapeutic advancements in spinal muscular atrophy

Spinal muscular atrophy (SMA) is an uncommon disorder associated with genes characterized by the gradual weakening and deterioration of muscles, often leading to substantial disability and premature mortality. Over the past decade, remarkable strides have been made in the field of SMA therapeutics,...

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Principais autores:	Pankaj Bagga, Sudhakar Singh, Gobind Ram, Subham Kapil, Avtar Singh
פורמט:	Artigo
שפה:	Inglês
יצא לאור:	Frontiers Media S.A. 2024-05-01
סדרה:	Frontiers in Neurology
נושאים:	spinal muscular atrophy survival motor neuron rehabilitation nusinersen onasemnogene abeparvovec risdiplam
גישה מקוונת:	https://www.frontiersin.org/articles/10.3389/fneur.2024.1368658/full
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