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Crizanlizumab in adult patients with sickle cell disease: a retrospective German analysis

IntroductionThe marketing authorization for crizanlizumab (Adakveo®), indicated for the prevention of recurrent vaso-occlusive crises (VOCs) in sickle cell patients (pts) aged ≥16, was revoked by the European Medicines Agency (EMA) as the STAND study did not demonstrate a significant difference betw...

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Autori principali: Friederike Poppenborg, Alexander Röth, Raina Yamamoto, Hans Christian Reinhardt, Ferras Alashkar
Natura: Artigo
Lingua:Inglês
Pubblicazione: Frontiers Media S.A. 2024-05-01
Serie:Frontiers in Hematology
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Accesso online:https://www.frontiersin.org/articles/10.3389/frhem.2024.1374181/full
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