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Feasibility, Safety, and Efficacy of Myoblast Transfer Therapy on Duchenne Muscular Dystrophy Boys

Five billion normal myoblasts were injected into each of 21 Duchenne muscular dystrophy (DMD) boys aged 6–14 yr to assess the feasibility, safety, and efficacy of the Phase II myoblast transfer therapy (MTT). The Phase II study was designed to strengthen muscles of both lower limbs. Forty-eight intr...

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Bibliografiska uppgifter
Huvudupphov: Peter K. Law, Tena G. Goodwin, Qiuwen Fang, Vijaya Duggirala, Charles Larkin, J. Ann Florendo, Dana S. Kirby, Mary Beth Deering, H.J. Li, Ming Chen, T.J. Yoo, Jennifer Cornett, Lawrence M. Li, Afshin Shirzad, Thomas Quinley, Randall L. Holcomb
Materialtyp: Artigo
Språk:Inglês
Utgiven: SAGE Publishing 1992-03-01
Serie:Cell Transplantation
Länkar:https://doi.org/10.1177/0963689792001002-305
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