A randomized crossover trial of elamipretide in adults with primary mitochondrial myopathy

Abstract Background This study aims to evaluate the effect of subcutaneous (SC) elamipretide dosing on exercise performance using the 6 min walk test (6MWT), patient‐reported outcomes measuring fatigue, functional assessments, and safety to guide the development of the Phase 3 trial. Methods MMPOWER...

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Autors principals:	Amel Karaa, Richard Haas, Amy Goldstein, Jerry Vockley, Bruce H. Cohen
Format:	Artigo
Idioma:	Inglês
Publicat:	Wiley 2020-08-01
Col·lecció:	Journal of Cachexia, Sarcopenia and Muscle
Matèries:	Myopathy Primary mitochondrial disease Elamipretide Exercise intolerance Primary mitochondrial myopathy Crossover trial
Accés en línia:	https://doi.org/10.1002/jcsm.12559
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