Gene therapy for selected neuromuscular and trinucleotide repeat disorders – An insight to subsume South Asia for multicenter clinical trials

Background: In this article, the authors discuss how they utilized the genetic mutation data in Sri Lankan Duchenne muscular dystrophy (DMD), Spinal muscular atrophy (SMA), Spinocerebellar ataxia (SCA) and Huntington’s disease (HD) patients and compare the available literature from South Asian count...

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ग्रंथसूची विवरण

मुख्य लेखकों:	Nalaka Wijekoon, Lakmal Gonawala, Pyara Ratnayake, Darshana Sirisena, Harsha Gunasekara, Athula Dissanayake, Sunethra Senanayake, Ajantha Keshavaraj, Yetrib Hathout, Harry W.M. Steinbusch, Chandra Mohan, Ashwin Dalal, Eric Hoffman, K.Ranil D de Silva
स्वरूप:	Artigo
भाषा:	Inglês
प्रकाशित:	Elsevier 2023-06-01
श्रृंखला:	IBRO Neuroscience Reports
विषय:	Indian Sub-continent Developing Countries Neurogenetic Disorders Bio Bank Duchenne Muscular Dystrophy Spinal Muscular Atrophy
ऑनलाइन पहुंच:	http://www.sciencedirect.com/science/article/pii/S266724212300009X
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