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Safety and efficacy of trofinetide in Rett syndrome: a systematic review and meta-analysis of randomized controlled trials

Abstract Introduction Rett syndrome is a rare genetic neurodevelopmental disorder that predominantly impacts females. It presents with loss of acquired skills, impaired communication, and stereotypic hand movements. Given the limited treatment options for Rett syndrome, there is a dire need for effe...

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Главные авторы: Abdallah Abbas, Aya M Fayoud, Mostafa Hossam El Din Moawad, Abdullah Ashraf Hamad, Heba Hamouda, Eman A. Fouad
Формат: Artigo
Язык:Inglês
Опубликовано: BMC 2024-03-01
Серии:BMC Pediatrics
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Online-ссылка:https://doi.org/10.1186/s12887-024-04526-3
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