Caregiver- and Clinician-Reported Symptoms in Pediatric Patients with Activated Phosphoinositide 3-Kinase Delta Syndrome (APDS) Receiving Leniolisib
IntroductionActivated Phosphoinositide 3-Kinase Delta Syndrome (APDS) is a rare disease characterized by early-onset, progressive symptoms. Delayed diagnosis and inadequate treatment in childhood may exacerbate disease manifestations and negatively impact health-related quality of life. In a 2-part,...
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| Autori principali: | , , , |
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| Natura: | Artigo |
| Lingua: | Inglês |
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Rockefeller University Press
2026-05-01
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| Serie: | Journal of Human Immunity |
| Accesso online: | https://rupress.org/jhi/article/2/CIS2026/eCIS2026abstract.34/281995/Caregiver-and-Clinician-Reported-Symptoms-in |
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