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Creatine/Creatinine Ratio and Myostatin as Biomarkers to Monitor Muscle Function in Duchenne Muscular Dystrophy Patients

ABSTRACT Background Duchenne Muscular Dystrophy (DMD) is characterized by progressive muscle wasting leading to early loss of motor function. Functional tests monitor disease progression and serve as clinical trial endpoints but are influenced by maturation in younger patients, high intra‐patient va...

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Principais autores: Chiara Degan, Roula Tsonaka, Sharon I. deVries, Nadine A. Ikelaar, Menno van derHolst, Hermien E. Kan, Erik H. Niks, Pietro Spitali
Formato: Artigo
Idioma:Inglês
Publicado em: Wiley 2026-06-01
coleção:Journal of Cachexia, Sarcopenia and Muscle
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Acesso em linha:https://doi.org/10.1002/jcsm.70320
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