Repeated Administrations of Human Umbilical Cord Blood Cells Improve Disease Outcomes in a Mouse Model of Sanfilippo Syndrome Type III B
Sanfilippo syndrome type III B (MPS III B) is an inherited disorder characterized by a deficiency of α- N -acetylglucosaminidase (Naglu) enzyme leading to accumulation of heparan sulfate in lysosomes and severe neurological deficits. We have previously shown that a single administration of human umb...
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| Hauptverfasser: | , , , , , , , , , |
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| Format: | Artigo |
| Sprache: | Inglês |
| Veröffentlicht: |
SAGE Publishing
2014-12-01
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| Schriftenreihe: | Cell Transplantation |
| Online-Zugang: | https://doi.org/10.3727/096368914X676916 |
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