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Modified-release hydrocortisone (Efmody®) in children with congenital adrenal hyperplasia: a retrospective registry study

BackgroundReplacement therapy for congenital adrenal hyperplasia (CAH) in childhood includes hydrocortisone and, in salt-wasting forms, addition of fludrocortisone. Immediate-release hydrocortisone often fails to adequately suppress early morning 17-hydroxyprogesterone (17OHP) levels. Hydrocortisone...

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Autors principals: Erwin Lankes, Levin Wiebelt, Kathrin Bettina Helge, Dirk Schnabel, Peter Kühnen, Oliver Blankenstein, Uta Neumann
Format: Artigo
Idioma:Inglês
Publicat: Frontiers Media S.A. 2026-07-01
Col·lecció:Frontiers in Endocrinology
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Accés en línia:https://www.frontiersin.org/articles/10.3389/fendo.2026.1854737/full
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