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Characteristics of drugs for ultra-rare diseases versus drugs for other rare diseases in HTA submissions made to the CADTH CDR

Abstract Background It has been suggested that ultra-rare diseases should be recognized as distinct from more prevalent rare diseases, but how drugs developed to treat ultra-rare diseases (DURDs) might be distinguished from drugs for ‘other’ rare diseases (DORDs) is not clear. We compared the charac...

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Збережено в:
Бібліографічні деталі
Автори: Trevor Richter, Ghayath Janoudi, William Amegatse, Sandra Nester-Parr
Формат: Artigo
Мова:Inglês
Опубліковано: BMC 2018-02-01
Серія:Orphanet Journal of Rare Diseases
Предмети:
Онлайн доступ:http://link.springer.com/article/10.1186/s13023-018-0762-1
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