Characteristics of drugs for ultra-rare diseases versus drugs for other rare diseases in HTA submissions made to the CADTH CDR
Abstract Background It has been suggested that ultra-rare diseases should be recognized as distinct from more prevalent rare diseases, but how drugs developed to treat ultra-rare diseases (DURDs) might be distinguished from drugs for ‘other’ rare diseases (DORDs) is not clear. We compared the charac...
Збережено в:
| Автори: | , , , |
|---|---|
| Формат: | Artigo |
| Мова: | Inglês |
| Опубліковано: |
BMC
2018-02-01
|
| Серія: | Orphanet Journal of Rare Diseases |
| Предмети: | |
| Онлайн доступ: | http://link.springer.com/article/10.1186/s13023-018-0762-1 |
| Теги: |
Немає тегів, Будьте першим, хто поставить тег для цього запису!
|
