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Transition to Emicizumab from standard-dose FVIII prophylaxis in young children with hemophilia A: a real-world study

Abstract Background Real-world evidence on transition from standard-dose FVIII to Emicizumab prophylaxis in young children with hemophilia A remains limited, particularly in developing countries. Methods We performed a single-center, retrospective, self-controlled study in boys with severe hemophili...

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Autors principals: Juan Ye, Kun Huang
Format: Artigo
Idioma:Inglês
Publicat: BMC 2026-05-01
Col·lecció:Thrombosis Journal
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Accés en línia:https://doi.org/10.1186/s12959-026-00868-3
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