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Up-front alternative donor HCT in severe aplastic anemia: gaps and opportunities to translate evidence into practice

Abstract: Severe aplastic anemia (SAA) is a rare and life-threatening bone marrow failure disorder. Immunosuppressive therapy (IST) with antithymocyte globulin and cyclosporine has long been a frontline treatment option in SAA; however, its limited durability and risk of long-term complications such...

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Egile Nagusiak: Neel S. Bhatt, Azra Borogovac, Yvonne A. Efebera, Anna DeSalvo, Steven M. Devine, Amy Foley, Valerie Greco-Stewart, Betty K. Hamilton, Mykala Heuer, Todd Molfenter, John P. Plastaras, Brittany K. Ragon, Sarah A. Wall, Larisa Broglie, Mark B. Juckett, Nandita Khera, Mary M. Horowitz, Amy E. DeZern
Formatua: Artigo
Hizkuntza:Inglês
Argitaratua: Elsevier 2025-09-01
Saila:Blood Advances
Sarrera elektronikoa:http://www.sciencedirect.com/science/article/pii/S2473952925003568
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