P004: Real-world clinical profiles of patients with alpha-mannosidosis: Baseline evaluations from the SPARKLE Registry

Slični predmeti

• P004: Real-world clinical profiles of patients with alpha-mannosidosis: Baseline evaluations from the SPARKLE Registry
  od: Nicole Muschol, i dr.
  Izdano: (2023-01-01)
• P244: Clinical profiles of 134 patients with alpha-mannosidosis from the velmanase alfa clinical program and SPARKLE registry
  od: Heather Morgan, i dr.
  Izdano: (2025-01-01)
• Evolution of mobility, pain/discomfort, self-care, and mental health in patients with alpha-mannosidosis: an international caregiver and patient survey
  od: Karolina M. Stepien, i dr.
  Izdano: (2025-05-01)
• Relationship between MAN2B1 genotype/subcellular localization subgroups, antidrug antibody detection, and long‐term velmanase alfa treatment outcomes in patients with alpha‐mannosidosis
  od: Line Gutte Borgwardt, i dr.
  Izdano: (2023-03-01)
• Health Related Quality of Life, Disability, and Pain in Alpha Mannosidosis
  od: Line Borgwardt MD, i dr.
  Izdano: (2018-09-01)