Impact of enzyme replacement therapy and migalastat on disease progression in females with fabry disease
Abstract Aim The aim of our multicenter study was to investigate the safety and efficacy of enzyme replacement therapy (ERT) and chaperone therapy on the disease progression in female Fabry disease (FD) patients and to compare the individual treatment regimens. Methods Data from 3 consecutive visits...
সংরক্ষণ করুন:
| প্রধান লেখক: | , , , , , , , |
|---|---|
| বিন্যাস: | Artigo |
| ভাষা: | Inglês |
| প্রকাশিত: |
BMC
2025-02-01
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| মালা: | Orphanet Journal of Rare Diseases |
| বিষয়গুলি: | |
| অনলাইন ব্যবহার করুন: | https://doi.org/10.1186/s13023-025-03600-y |
| ট্যাগগুলো: |
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