Tryngolza (Olezarsen)
Familial chylomicronemia syndrome (FCS) is a rare autosomal recessive disorder caused by mutations in the lipoprotein lipase gene, resulting in severe hypertriglyceridemia and life-threatening complications such as acute pancreatitis. Tryngolza (olezarsen) is a novel antisense oligonucleotide therap...
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| Autors principals: | , |
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| Format: | Artigo |
| Idioma: | Inglês |
| Publicat: |
Wolters Kluwer Medknow Publications
2025-07-01
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| Col·lecció: | Amrita Journal of Medicine |
| Matèries: | |
| Accés en línia: | https://doi.org/10.4103/AMJM.AMJM_33_25 |
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