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Novel Translational Concept: Axon-to-Muscle Exosomal Signaling as an Emerging Therapeutic Target in Spinal Muscular Atrophy

Spinal muscular atrophy (SMA) has transitioned from a uniformly fatal disease to a treatable condition, yet incomplete neuromuscular recovery underscores the limits of current SMN-restorative therapies. Emerging data implicate disrupted axon-to-muscle exosomal signaling as an important, overlooked d...

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Principais autores: Almir Fajkić, Andrej Belančić, Yun Wah Lam, Valentino Rački, Kristina Pilipović, Tamara Janković, Silvestar Mežnarić, Jasenka Mršić-Pelčić, Dinko Vitezić
格式: Artigo
語言:Inglês
出版: MDPI AG 2025-11-01
叢編:Biomedicines
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在線閱讀:https://www.mdpi.com/2227-9059/13/12/2876
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