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Treatment characteristics of patients with hereditary transthyretin amyloidosis: a cohort study

Abstract Background There are novel medications approved for the treatment of hereditary transthyretin amyloidosis (ATTRv), classified as transthyretin (TTR) stabilizers or gene silencers. While many patients may be on both classes of medications, there is no data available on the safety and efficac...

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Bibliografiset tiedot
Päätekijät: Taha N. Qarni, Felipe J. S. Jones, Brian Drachman, Sami Khella, Janice Pieretti, Nicolas Sarmiento Bustamante, Chafic Karam
Aineistotyyppi: Artigo
Kieli:Inglês
Julkaistu: BMC 2024-05-01
Sarja:Orphanet Journal of Rare Diseases
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Linkit:https://doi.org/10.1186/s13023-024-03198-7
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