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Antisense oligonucleotides and their applications in rare neurological diseases

Rare diseases affect almost 500 million people globally, predominantly impacting children and often leading to significantly impaired quality of life and high treatment costs. While significant contributions have been made to develop effective treatments for those with rare diseases, more rapid drug...

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Principais autores: Simon McDowall, May Aung-Htut, Steve Wilton, Dunhui Li
Formato: Artigo
Idioma:Inglês
Publicado em: Frontiers Media S.A. 2024-09-01
coleção:Frontiers in Neuroscience
Assuntos:
Acesso em linha:https://www.frontiersin.org/articles/10.3389/fnins.2024.1414658/full
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