Screening for calcium channel modulators in CLN3 siRNA knock down SH-SY5Y neuroblastoma cells reveals a significant decrease of intracellular calcium levels by selected L-type calc...

Por an Haack, Kristina, Narayan, Srinivas B., Li, Haying, Warnock, Ashley, Tan, Lu, Bennett, Michael J.
Publicado em 2010

Forced vital capacity and cross-domain late-onset Pompe disease outcomes: an individual patient-level data meta-analysis

Por Berger, Kenneth I., Kanters, Steve, Jansen, Jeroen P., Stewart, Andrew, Sparks, Susan, Haack, Kristina An, Bolzani, Anna, Siliman, Gaye, Hamed, Alaa
Publicado no J Neurol (2019)

Development and content validation of the Pediatric Oral Medicines Acceptability Questionnaires (P-OMAQ): patient-reported and caregiver-reported outcome measures

Por Turner-Bowker, Diane M., An Haack, Kristina, Krohe, Meaghan, Yaworsky, Andrew, Vivas, Norma, Kelly, Masami, Chatterjee, Godhuli, Chaston, Emily, Mann, Erin, Reaney, Matthew
Publicado no J Patient Rep Outcomes (2020)

How is the Pharmaceutical Industry Structured to Optimize Pediatric Drug Development? Existing Pediatric Structure Models and Proposed Recommendations for Structural Enhancement

Por Severin, Thomas, Corriol-Rohou, Solange, Bucci-Rechtweg, Christina, an Haack, Kristina, Fuerst-Recktenwald, Sabine, Lepola, Pirkko, Norjavaara, Ensio, Dehlinger-Kremer, Martine, Haertter, Sebastian, Cheung, S. Y. Amy
Publicado no Ther Innov Regul Sci (2020)

Correction to: How is the Pharmaceutical Industry Structured to Optimize Pediatric Drug Development? Existing Pediatric Structure Models and Proposed Recommendations for Structural...

Por Severin, Thomas, Corriol-Rohou, Solange, Bucci-Rechtweg, Christina, an Haack, Kristina, Fuerst-Recktenwald, Sabine, Lepola, Pirkko, Norjavaara, Ensio, Dehlinger-Kremer, Martine, Haertter, Sebastian, Cheung, S. Y. Amy
Publicado no Ther Innov Regul Sci (2020)

Characterization of Early Disease Status in Treatment-Naive Male Paediatric Patients with Fabry Disease Enrolled in a Randomized Clinical Trial

Por Wijburg, Frits A., Bénichou, Bernard, Bichet, Daniel G., Clarke, Lorne A., Dostalova, Gabriela, Fainboim, Alejandro, Fellgiebel, Andreas, Forcelini, Cassiano, An Haack, Kristina, Hopkin, Robert J., Mauer, Michael, Najafian, Behzad, Scott, C. Ronald, Shankar, Suma P., Thurberg, Beth L., Tøndel, Camilla, Tylki-Szymańska, Anna, Ramaswami, Uma
Publicado no PLoS One (2015)