Improvement of Fabry Disease-Related Gastrointestinal Symptoms in a Significant Proportion of Female Patients Treated with Agalsidase Beta: Data from the Fabry Registry

Por Wilcox, William R., Feldt-Rasmussen, Ulla, Martins, Ana Maria, Ortiz, Alberto, Lemay, Roberta M., Jovanovic, Ana, Germain, Dominique P., Varas, Carmen, Nicholls, Katherine, Weidemann, Frank, Hopkin, Robert J.
Publicado no JIMD Rep (2017)

Utility of Rare Disease Registries in Latin America

Por Martins, Ana Maria, Kerstenezky, Marcelo, Linares, Adriana, Politei, Juan, Kohan, Regina, Ospina, Sandra, Varas, Carmen, Villalobos, Jacobo, Amartino, Hernán, Franco, Sergio, Valadez, Guilhermo, Giugliani, Roberto, Guerra, Patricio, Sanches, Luz
Publicado em 2011