Effects of Growth Hormone Treatment in Adults with Prader-Willi Syndrome

nork Butler, M.G., Smith, B.K., Lee, J., Gibson, C., Schmoll, C., Moore, W.V., Donnelly, J.E.
Argitaratua 2013

Advancements in AAV-mediated Gene Therapy for Pompe Disease

nork Salabarria, S.M., Nair, J., Clement, N., Smith, B.K., Raben, N., Fuller, D.D., Byrne, B.J., Corti, M.
Argitaratua izan da J Neuromuscul Dis (2020)

Weight management for individuals with intellectual and developmental disabilities: Rationale and design for an 18 month randomized trial

nork Donnelly, JE, Saunders, RR, Saunders, M, Washburn, RA, Sullivan, DK, Gibson, CA, Ptomey, LT, Goetz, JR, Honas, JJ, Betts, JL, Rondon, MR, Smith, BK, Mayo, MS
Argitaratua 2013

B-cell depletion is protective against anti-AAV capsid immune response: a human subject case study

nork Corti, M, Elder, ME, Falk, DJ, Lawson, L, Smith, BK, Nayak, S, Conlon, TJ, Clément, N, Erger, K, Lavassani, E, Green, MM, Doerfler, PA, Herzog, RW, Byrne, BJ
Argitaratua izan da Mol Ther Methods Clin Dev (2014)