Substrate Deprivation Therapy to Reduce Glycosaminoglycan Synthesis Improves Aspects of Neurological and Skeletal Pathology in MPS I Mice

Por Derrick-Roberts, Ainslie L. K., Jackson, Matilda R., Pyragius, Carmen E., Byers, Sharon
Publicado no Diseases (2017)

Gene silencing of EXTL2 and EXTL3 as a substrate deprivation therapy for heparan sulphate storing mucopolysaccharidoses

Por Kaidonis, Xenia, Liaw, Wan Chin, Roberts, Ainslie Derrick, Ly, Marleesa, Anson, Donald, Byers, Sharon
Publicado em 2010

Lentiviral-mediated gene correction of mucopolysaccharidosis type IIIA

Por Anson, Donald S, McIntyre, Chantelle, Thomas, Belinda, Koldej, Rachel, Ranieri, Enzo, Roberts, Ainslie, Clements, Peter R, Dunning, Kylie, Byers, Sharon
Publicado em 2007