CRISPR-Cas9 Gene Editing of Hematopoietic Stem Cells from Patients with Friedreich’s Ataxia

由 Rocca, Celine J., Rainaldi, Joseph N., Sharma, Jay, Shi, Yanmeng, Haquang, Joseph H., Luebeck, Jens, Mali, Prashant, Cherqui, Stephanie
發表在 Mol Ther Methods Clin Dev (2020)