Observational study of spinal muscular atrophy type I and implications for clinical trials

بواسطة Finkel, Richard S., McDermott, Michael P., Kaufmann, Petra, Darras, Basil T., Chung, Wendy K., Sproule, Douglas M., Kang, Peter B., Foley, A. Reghan, Yang, Michelle L., Martens, William B., Oskoui, Maryam, Glanzman, Allan M., Flickinger, Jean, Montes, Jacqueline, Dunaway, Sally, O'Hagen, Jessica, Quigley, Janet, Riley, Susan, Benton, Maryjane, Ryan, Patricia A., Montgomery, Megan, Marra, Jonathan, Gooch, Clifton, De Vivo, Darryl C.
منشور في 2014

Observational Study of Spinal Muscular Atrophy Type 2 and 3: Functional Outcomes Over 1 Year

بواسطة Kaufmann, Petra, McDermott, Michael P., Darras, Basil T., Finkel, Richard, Kang, Peter, Oskoui, Maryam, Constantinescu, Andrei, Sproule, Douglas Michael, Foley, A. Reghan, Yang, Michele, Tawil, Rabi, Chung, Wendy, Martens, Bill, Montes, Jacqueline, O'Hagen, Jessica, Dunaway, Sally, Flickinger, Jean M., Quigley, Janet, Riley, Susan, Glanzman, Allan M., Benton, Maryjane, Ryan, Patricia A., Irvine, Carrie, Annis, Christine L., Butler, Hailly, Caracciolo, Jayson, Montgomery, Megan, Marra, Jonathan, Koo, Benjamin, De Vivo, Darryl C.
منشور في 2011

Prospective cohort study of spinal muscular atrophy types 2 and 3

بواسطة Kaufmann, Petra, McDermott, Michael P., Darras, Basil T., Finkel, Richard S., Sproule, Douglas M., Kang, Peter B., Oskoui, Maryam, Constantinescu, Andrei, Gooch, Clifton L., Foley, A. Reghan, Yang, Michele L., Tawil, Rabi, Chung, Wendy K., Martens, William B., Montes, Jacqueline, Battista, Vanessa, O'Hagen, Jessica, Dunaway, Sally, Flickinger, Jean, Quigley, Janet, Riley, Susan, Glanzman, Allan M., Benton, Maryjane, Ryan, Patricia A., Punyanitya, Mark, Montgomery, Megan J., Marra, Jonathan, Koo, Benjamin, De Vivo, Darryl C.
منشور في 2012