Pancreatic Transduction by Helper-Dependent Adenoviral Vectors via Intraductal Delivery

Por Morró, Meritxell, Teichenne, Joan, Jimenez, Veronica, Kratzer, Ramona, Marletta, Serena, Maggioni, Luca, Mallol, Cristina, Ruberte, Jesus, Kochanek, Stefan, Bosch, Fatima, Ayuso, Eduard
Publicado em 2014

CNS-directed gene therapy for the treatment of neurologic and somatic mucopolysaccharidosis type II (Hunter syndrome)

Por Motas, Sandra, Haurigot, Virginia, Garcia, Miguel, Marcó, Sara, Ribera, Albert, Roca, Carles, Sánchez, Xavier, Sánchez, Víctor, Molas, Maria, Bertolin, Joan, Maggioni, Luca, León, Xavier, Ruberte, Jesús, Bosch, Fatima
Publicado no JCI Insight (2016)

Whole body correction of mucopolysaccharidosis IIIA by intracerebrospinal fluid gene therapy

Por Haurigot, Virginia, Marcó, Sara, Ribera, Albert, Garcia, Miguel, Ruzo, Albert, Villacampa, Pilar, Ayuso, Eduard, Añor, Sònia, Andaluz, Anna, Pineda, Mercedes, García-Fructuoso, Gemma, Molas, Maria, Maggioni, Luca, Muñoz, Sergio, Motas, Sandra, Ruberte, Jesús, Mingozzi, Federico, Pumarola, Martí, Bosch, Fatima
Publicado em 2013