Safe and Efficient Gene Therapy for Pyruvate Kinase Deficiency

Por Garcia-Gomez, Maria, Calabria, Andrea, Garcia-Bravo, Maria, Benedicenti, Fabrizio, Kosinski, Penelope, López-Manzaneda, Sergio, Hill, Collin, del Mar Mañu-Pereira, María, Martín, Miguel A, Orman, Israel, Vives-Corrons, Joan-LLuis, Kung, Charles, Schambach, Axel, Jin, Shengfang, Bueren, Juan A, Montini, Eugenio, Navarro, Susana, Segovia, Jose C
Publicado no Mol Ther (2016)