AAVrh10 Gene Therapy Ameliorates Central and Peripheral Nervous System Disease in Canine Globoid Cell Leukodystrophy (Krabbe Disease)

Por Bradbury, Allison M., Rafi, Mohammed A., Bagel, Jessica H., Brisson, Becky K., Marshall, Michael S., Pesayco Salvador, Jill, Jiang, Xuntain, Swain, Gary P., Prociuk, Maria L., ODonnell, Patricia A., Fitzgerald, Caitlin, Ory, Daniel S., Bongarzone, Ernesto R., Shelton, G. Diane, Wenger, David A., Vite, Charles H.
Publicado no Hum Gene Ther (2018)