Gene Editing for Duchenne Muscular Dystrophy Using the CRISPR/Cas9 Technology: The Importance of Fine-tuning the Approach

Por Tremblay, Jacques P, Iyombe-Engembe, Jean-Paul, Duchêne, Benjamin, Ouellet, Dominique L
Publicado no Mol Ther (2016)

Efficient Restoration of the Dystrophin Gene Reading Frame and Protein Structure in DMD Myoblasts Using the CinDel Method

Por Iyombe-Engembe, Jean-Paul, Ouellet, Dominique L, Barbeau, Xavier, Rousseau, Joël, Chapdelaine, Pierre, Lagüe, Patrick, Tremblay, Jacques P
Publicado no Mol Ther Nucleic Acids (2016)