Engineered mutant α-ENaC subunit mRNA delivered by lipid nanoparticles reduces amiloride currents in cystic fibrosis–based cell and mice models

af Mukherjee, Anindit, MacDonald, Kelvin D., Kim, Jeonghwan, Henderson, Michael I., Eygeris, Yulia, Sahay, Gaurav
Udgivet i Sci Adv (2020)