Computationally designed liver-specific transcriptional modules and hyperactive factor IX improve hepatic gene therapy

Por Nair, Nisha, Rincon, Melvin Y., Evens, Hanneke, Sarcar, Shilpita, Dastidar, Sumitava, Samara-Kuko, Emira, Ghandeharian, Omid, Man Viecelli, Hiu, Thöny, Beat, De Bleser, Pieter, VandenDriessche, Thierry, Chuah, Marinee K.
Publicado em 2014